Recruiting Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH NCT02716246 Conditions Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more Locations Nationwide Children's Hospital — Columbus, Ohio, United States Children's Hospital of Pittsburgh — Pittsburgh, Pennsylvania, United States Women's and Children's Hospital — North Adelaide, South Australia, Australia Vall d'Hebron Barcelona Hospital Campus — Barcelona, Spain View more locations Show fewer locations Loading locations... View Trial Details
Enrolling by Invitation Follow-up Study of AAV-Mediated Gene Transfer (UX111; Previously Known as ABO-102) for MPS Type IIIA NCT04360265 Conditions Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +13 more Locations Nationwide Children's Hospital — Columbus, Ohio, United States Women's and Children's Hospital — North Adelaide, South Australia, Australia Vall d'Hebron Barcelona Campus — Barcelona, Spain Hospital Clínico Universitario de Santiago — Santiago de Compostela, Spain View Trial Details
