Recruiting Melpida: Recombinant Adeno-associated Virus (Serotype 9) Encoding a Codon Optimized Human AP4M1 Transgene (hAP4M1opt) NCT05518188 Conditions Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, +21 more Locations Children's Medical Center Dallas — Dallas, Texas, United States View Trial Details
Recruiting Registry and Natural History Study for Early Onset Hereditary Spastic Paraplegia NCT04712812 Conditions AP4-related Hereditary Spastic Paraplegia, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +26 more Locations Boston Children's Hospital — Boston, Massachusetts, United States View Trial Details
