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Recruiting
Invasive Home Ventilation in Denmark
NCT07467187
- Conditions
- ALS (Amyotrophic Lateral Sclerosis), Amyotrophic Lateral Sclerosis, Autonomic Nervous System Diseases, +38 more
- Locations
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- Respiratory Center East Copenhagen, Denmark
NCT06971094
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
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- The Seventh Medical Center of Chinese PLA General Hospital Beijing, China
- Children's Medical Center of Peking University First Hospital Beijing, China
- Beijing Children's Hospital, Capital Medical University Beijing, China
- National Children's Medical Center,Shanghai Jiaotong University Shanghai, China
Not Yet Recruiting
Adrenal& Bone Complications in Paediatric Patients Living With Spinal Muscular Atrophy (SMA)
NCT07530926
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- Sheffield Children's NHS Foundation Trust Sheffield, South Yorkshire, United Kingdom
Completed
Gene Replacement Therapy Clinical Trial for Participants With Spinal Muscular Atrophy Type 1
NCT03306277
- Conditions
- Central Nervous System Diseases, Gene Therapy, Motor Neuron Disease, +6 more
- Locations
-
- David Geffen School of Medicine at UCLA Los Angeles, California, United States
- Stanford University Stanford, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Nemours Children's Hospital Orlando, Florida, United States
Active, Not Recruiting
HABIT-ILE + FST in Children With SMA
NCT07223320
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- Center for Cerebral Palsy Research, Teachers College, Columbia University New York, United States