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Published and searchable clinical trials
NCT07047144
- Conditions
- Anti-myostatin, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +17 more
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Children's Hospital of Orange County (CHOC) Orange, California, United States
- Stanford Neuroscience Health Center (SNHC) Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
Swiss Registry for Neuromuscular Disorders
NCT05102916
- Conditions
- BMD, Congenital Muscular Dystrophy, DMD, +2 more
- Locations
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- Cantonal Hospital Aarau Aarau, Canton of Aargau, Switzerland
- Pediatric Institute of Southern Switzerland, Ospedale San Giovanni Bellinzona, Canton Ticino, Switzerland
- Neuro Centre of Italian Switzerland, Ospedale Regionale di Lugano Lugano, Canton Ticino, Switzerland
- University Hospital Lausanne CHUV, Children's Hospital Lausanne, Vaude, Switzerland
UK SMA Patient Registry
NCT04292574
- Conditions
- Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
-
- John Walton Muscular Dystrophy Research Centre Newcastle upon Tyne, United Kingdom
NCT06322654
- Conditions
- SMA
- Locations
-
- Wiktor Dega University Orthopedic and Rehabilitation Hospital Poznan, Poland
NCT07321990
- Conditions
- SMA
- Locations
-
- Association institut de Myologie Paris, France
NCT03461289
- Conditions
- SMA
- Locations
-
- University Hospital Ghent Neuromuscular reference center Ghent, Belgium
- Neuropédiatrie - Centre de Référence des Maladies Neuromusculaires Liège, Belgium
- Hôpital Armand Trousseau Paris, France
- Istituto Gianninia Gaslini Genova, Italy
NCT05156320
- Conditions
- Anti-myostatin, Atrophy, Central Nervous System Diseases, +20 more
- Locations
-
- Children's of Alabama Birmingham, Alabama, United States
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Children's Hospital of Los Angeles Los Angeles, California, United States
- Stanford University Medical Center Palo Alto, California, United States
An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy
NCT03921528
- Conditions
- Atrophy, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +19 more
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Stanford University Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- The Johns Hopkins University Baltimore, Maryland, United States
NCT02941328
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +12 more
- Locations
-
- University Medical Center of Utrecht (UMCU) Utrecht, Netherlands
NCT01984957
- Conditions
- ALS, Motor Neuron Disease, Nervous System Diseases, +4 more
- Locations
-
- Centre d'évaluation Thérapeutique, Dr LACOMBLEZ Paris, France
NCT00774423
- Conditions
- SMA
- Locations
-
- Hopital Raymond Poincare Garches, France
A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy
NCT05337553
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +6 more
- Locations
-
- Phoenix Children's Phoenix, Arizona, United States
- UCSD & Rady Children's La Jolla, California, United States
- Children's Hospital of Los Angeles Los Angeles, California, United States
- UCSF Benioff Children's Hospital, Medical Center San Francisco, California, United States
Spinal Cord Stimulation for the Treatment of Motor Deficits in People With Spinal Muscular Atrophy - Upper Limb
NCT06300996
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +14 more
- Locations
-
- University of Pittsburgh Pittsburgh, Pennsylvania, United States
Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab
NCT05626855
- Conditions
- Anti-myostatin, Atrophy, Central Nervous System Diseases, +20 more
- Locations
-
- Phoenix Childrens Hospital Phoenix, Arizona, United States
- UCSD Altman Clinical and Translational Research La Jolla, California, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
- Stanford Neuroscience Health Center Palo Alto, California, United States
Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi
NCT04042025
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +12 more
- Locations
-
- Stanford University Medical Center Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Ann Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- John Hopkins Hospital - David M. Rubenstein Child Health Building Baltimore, Maryland, United States