Recruiting JAG201 Gene Therapy Study in Children & Adults With SHANK3 Haploinsufficiency NCT06662188 Conditions Phelan-McDermid Syndrome, SHANK3 Haploinsufficiency, Telomeric 22q13 Monosomy Syndrome Locations Rush University — Chicago, Illinois, United States Boston Children's Hospital — Boston, Massachusetts, United States Seaver Autism Center at Mount Sinai — New York, United States View Trial Details
Enrolling by Invitation Long-Term Follow-Up Study for RB001 Gene Therapy Study in Children With SHANK3-related Phelan McDermid Syndrome (PMS) NCT07690527 Conditions Phelan-McDermid Syndrome, SHANK3 Haploinsufficiency, Telomeric 22q13 Monosomy Syndrome Locations Peking University First Hospital — Beijing, China View Trial Details
Active, Not Recruiting RB001 Gene Therapy Study in Children With SHANK3-related Phelan-McDermid Syndrome (PMS) NCT07014020 Conditions Phelan-McDermid Syndrome, SHANK3 Haploinsufficiency, Telomeric 22q13 Monosomy Syndrome Locations Peking University First Hospital — Beijing, Beijing Municipality, China View Trial Details
