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NCT06789445
- Conditions
- Abnormalities, Multiple, Blindness, Cone-Rod Disease (C-RD), +31 more
- Locations
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- University of Southern California /Children's Hospital of Los Angeles Los Angeles, California, United States
- University of Miami, Bascom Palmer Eye Institute Miami, Florida, United States
- Mid Atlantic Retina/ Wills Eye Philadelphia, Pennsylvania, United States
- Retina Foundation of the Southwest Dallas, Texas, United States
NCT02320812
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Eye Diseases, Hereditary, +6 more
- Locations
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- The Gavin Herbert Eye Institute, Univ California Irvine Irvine, California, United States
- Retina-Vitreous Associates Medical Group Los Angeles, California, United States
Completed
Natural History Study in Inherited Retinal Disease Subjects Caused by Mutations in RPE65 or LRAT
NCT02575430
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Eye Diseases, Hereditary, +8 more
- Locations
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- Wilmer Eye Institute - Johns Hopkins Hospital Baltimore, Maryland, United States
- Casey Eye Institute - Marquam Hill Portland, Oregon, United States
- The Hospital for Sick Children, Ophthalmology and Vision Sciences Toronto, Ontario, Canada
- Montreal Children's Hospital, McGill University Health Centre Montreal, Quebec, Canada
Active, Not Recruiting
Study to Evaluate Ultevursen in Subjects With Retinitis Pigmentosa (RP) Due to Mutations in Exon 13 of the USH2A Gene
NCT06627179
- Conditions
- Abnormalities, Multiple, Blindness, Congenital Abnormalities, +28 more
- Locations
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- The University of California, San Francisco San Francisco, California, United States
- Bascom Palmer Eye Institute/University of Miami Miami, Florida, United States
- Emory University Atlanta, Georgia, United States
- Massachusetts Eye and Ear Boston, Massachusetts, United States