Completed Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid NCT00007020 Conditions Abnormalities, Multiple, Adrenal Gland Diseases, Adrenal Insufficiency, +37 more Locations Cincinnati Children's Hospital Medical Center — Cincinnati, Ohio, United States View Trial Details
Completed Betaine and Peroxisome Biogenesis Disorders NCT01838941 Conditions Abnormalities, Multiple, Brain Diseases, Brain Diseases, Metabolic, +22 more Locations Montreal Children's Hospital — Montreal, Quebec, Canada View Trial Details
Active, Not Recruiting MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis NCT02171104 Conditions Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more Locations Masonic Cancer Center, University of Minnesota — Minneapolis, Minnesota, United States View Trial Details