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Showing 1–20 of 466 trials

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Published and searchable clinical trials

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Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Genetic Disease, +5 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • HudsonAlpha Institute for Biotechnology, Inc. Huntsville, Alabama, United States
  • University of California, Los Angeles Los Angeles, California, United States
  • University of California, Irvine Medical Center Orange, California, United States
View all 33 locations
Conditions
Disease Attributes, Inborn Errors of Metabolism Disorders, Orphan Diseases, +5 more
Locations
  • Medical University of Graz Graz, Austria
  • Medical University of Innsbruck Innsbruck, Austria
  • The Faculty of Medicine JKU Linz Linz, Austria
  • SALK PMU Salzburg, Austria
Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Duchene Muscular Dystrophy, +12 more
Locations
  • Arkansas Children's Research Institute Little Rock, Arkansas, United States
  • Children's National Hospital Washington D.C., District of Columbia, United States
  • Ann and Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +17 more
Locations
  • University of California - Irvine Medical Center Irvine, California, United States
  • University of Florida (UF) - Gainesville Gainesville, Florida, United States
  • Emory University Hospital Atlanta, Georgia, United States
  • Washington University in St. Louis St Louis, Missouri, United States
View all 28 locations
Conditions
Ataxia, Brain Diseases, Central Nervous System Diseases, +21 more
Locations
  • The University of California, Los Angeles (UCLA) Los Angeles, California, United States
  • The Ohio State University Columbus, Ohio, United States
  • The Children's Hospital of Philadelphia (CHOP) Philadelphia, Pennsylvania, United States