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Showing 1–13 of 13 trials
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Published and searchable clinical trials
High-Dose Vitamin C in G6PDA and Pyruvate Kinase Deficiency: A Safety Study
NCT07612345
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +12 more
- Locations
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- University of Utah Salt Lake City, Utah, United States
NCT04902833
- Conditions
- Acute Myeloid Leukemia, Anemia, Anemia, Hemolytic, +24 more
- Locations
-
- Massachusetts General Hospital Boston, Massachusetts, United States
NCT02476916
- Conditions
- Anemia, Anemia, Hemolytic, Hematologic Diseases, +3 more
- Locations
-
- Stanford University Palo Alto, California, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Wayne State University School of Medicine - Children's Hospital of Michigan Detroit, Michigan, United States
- New York Presbyterian Hospital- Weil Cornell Medical College New York, United States
NCT03853798
- Conditions
- Pyruvate Kinase Deficiency, Pyruvate Kinase Deficiency of Red Cells
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- UCSF Benioff Children's Hospital, Oakland Oakland, California, United States
- Emory-Children's Center Atlanta, Georgia, United States
- Indiana Hemophilia & Thrombosis Center Inc. Indianapolis, Indiana, United States
NCT04105166
- Conditions
- Anemia, Anemia, Hemolytic, Hematologic Diseases, +3 more
- Locations
-
- Stanford University Stanford, California, United States
- Hospital Infantil Universitario Niño Jesús Madrid, Spain
- Hospital Universitario Fundación Jiménez Díaz Madrid, Spain
NCT04995315
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
- Locations
-
- Massachusetts General Hospital Boston, Massachusetts, United States
- Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico Milan, Italy
- Universitair Medisch Centrum Utrecht Utrecht, Netherlands
NCT03866590
- Conditions
- Pyruvate Kinase Deficiency, Pyruvate Kinase Deficiency of Red Cells
- Locations
-
- Intervent Clinical Research Center Pembroke Pines, Florida, United States
NCT03548220
- Conditions
- Anemia, Anemia, Hemolytic, Hematologic Diseases, +3 more
- Locations
-
- University of Arkansas for Medical Sciences Little Rock, Arkansas, United States
- Emory University Atlanta, Georgia, United States
- Indiana Hemophilia and Thrombosis Center Indianapolis, Indiana, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
NCT03559699
- Conditions
- Anemia, Anemia, Hemolytic, Hematologic Diseases, +3 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland, California, United States
- Emory University Atlanta, Georgia, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
- Seattle Cancer Care Alliance Seattle, Washington, United States
NCT02053480
- Conditions
- Anemia, Anemia, Hemolytic, Congenital Non-Spherocytic Hemolytic Anemia, +10 more
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Stanford University Palo Alto, California, United States
- Children's Hospital of Atlanta Atlanta, Georgia, United States
- Lurie Children's Hospital Chicago, Illinois, United States
Pyruvate Kinase Deficiency Global Longitudinal Registry
NCT03481738
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
- Locations
-
- Phoenix Childrens Hospital Phoenix, Arizona, United States
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- University of Arkansas for Medical Sciences Little Rock, Arkansas, United States
- Children's Hospital of Orange County Orange, California, United States
A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Not Regularly Transfused, Followed by a 5-Year Extension Period
NCT05175105
- Conditions
- Anemia, Hematologic Diseases, Hemic and Lymphatic Diseases, +5 more
- Locations
-
- Stanford Medicine Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Children's Healthcare of Atlanta - Emory Atlanta, Georgia, United States
- UChicago Medicine Chicago, Illinois, United States
A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Regularly Transfused, Followed by a 5-Year Extension Period
NCT05144256
- Conditions
- Anemia, Hematologic Diseases, Hemic and Lymphatic Diseases, +5 more
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Stanford Medicine Palo Alto, California, United States
- Children's Healthcare of Atlanta - Emory Atlanta, Georgia, United States
- Boston Children's Hospital Boston, Massachusetts, United States