Recruiting Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency NCT06340685 Conditions Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more Locations UPMC Children's Hospital of Pittsburgh — Pittsburgh, Pennsylvania, United States View Trial Details
Completed Use of Phenylbutyrate Therapy for Patients With Pyruvate Dehydrogenase Complex Deficiency. NCT03734263 Conditions Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more Locations Federico II University — Naples, Italy View Trial Details
Active, Not Recruiting Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency: NCT02616484 Conditions Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more Locations Children's Hospital of Orange County — Orange, California, United States Stanford University — Stanford, California, United States Children's National Medical Center — Washington D.C., District of Columbia, United States University of Florida — Gainesville, Florida, United States View more locations Show fewer locations Loading locations... View Trial Details