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NCT03333200
- Conditions
- ALD, Alpha-Mannosidosis, Batten Disease, +78 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT06092346
- Conditions
- ADA2 protein, human, ADA2, OMIM *607575,Sneddon Syndrome; VAIHS, ADSL, OMIM *608222, Adenylosuccinate Lyase Deficiency, +84 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT00008450
- Conditions
- Adenosine Deaminase Deficiency, Autosomal Recessive Disorder, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +17 more
- Locations
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- Fred Hutch/University of Washington Cancer Consortium Seattle, Washington, United States