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Phase I/II Trial of Everolimus in Combination With Lonafarnib in Progeria
NCT02579044
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Laminopathies, +4 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States
NCT04512963
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, Genetic Diseases, Inborn, +7 more
- Locations
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- PRG S&T Investigational Site Glendale, California, United States
Completed
Clinical Studies of Progeria
NCT00094393
- Conditions
- Aging, Premature, Arterial Occlusive Diseases, Arteriosclerosis, +25 more
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
NCT00425607
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hutchinson-Gilford Syndrome, +5 more
- Locations
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- Children's Hospital Boston Boston, Massachusetts, United States
NCT00879034
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hutchinson-Gilford Syndrome, +5 more
- Locations
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- Children's Hospital Boston Boston, Massachusetts, United States
Active, Not Recruiting
Study to Determine Optimal Dose and Evaluate Safety, Tolerability, and Pharmacokinetics of Progerinin in Patients With Hutchinson-Gilford Progeria Syndrome (HGPS)
NCT06775041
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hutchinson-Gilford Progeria Syndrome, +5 more
- Locations
-
- Boston Children's Hospital Boston, Massachusetts, United States