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Enrolling by Invitation
Open-Label Extension Study to Assess GLM101 in PMM2-CDG Patients
NCT06657859
- Conditions
- Congenital disorder of glycosylation type 1A, PMM2-CDG, Phosphomannomutase 2 Deficiency
- Locations
-
- University of Minnesota Minneapolis, Minnesota, United States
- The Icahn School of Medicine at Mount Sinai New York, United States
- The Children's Hospital of Philadelphia (CHOP) Philadelphia, Pennsylvania, United States
- Seattle Children's Hospital Seattle, Washington, United States
NCT03173300
- Conditions
- Congenital disorder of glycosylation type 1A, Phosphomannomutase 2 Deficiency
- Locations
-
- Mayo Clinic College of Medicine Rochester, Minnesota, United States
- Children's Hospital of Philadelphia (CHOP) Philadelphia, Pennsylvania, United States
- Seattle Children's Hospital Seattle, Washington, United States
- University Hospital Leuven Leuven, Belgium
Completed
24-Week Study to Assess the PD, Safety, Tolerability, and PK of GLM101 in Participants With PMM2-CDG
NCT05549219
- Conditions
- Congenital disorder of glycosylation type 1A, PMM2-CDG, Phosphomannomutase 2 Deficiency
- Locations
-
- Clinical Research of West Florida Tampa, Florida, United States
- Mayo Clinic Rochester, Minnesota, United States
- Hospital Sant Joan de Déu Barcelona, Spain
- Great Ormond Street Hospital London, United Kingdom
Active, Not Recruiting
A Study to Assess the Efficacy and Safety of Weekly Doses of GLM101 in Participants With PMM2-CDG
NCT06892288
- Conditions
- Ataxia, Congenital disorder of glycosylation type 1A, Dyskinesias, +6 more
- Locations
-
- University of Minnesota Minneapolis, Minnesota, United States
- Icahn School of Medicine at Mount Sinai New York, United States
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- Seattle Children's Hospital Seattle, Washington, United States