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Published and searchable clinical trials
NCT06325709
- Conditions
- Chronic Disease, Chronic Granulomatous Disease (CGD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT00001405
- Conditions
- Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, +18 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT00006150
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Hematologic Diseases, +13 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT05189925
- Conditions
- Chronic Disease, Chronic Granulomatous Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +16 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Study of Chediak-Higashi Syndrome
NCT00005917
- Conditions
- Albinism, Amino Acid Metabolism, Inborn Errors, Blood Coagulation Disorders, +24 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT00128973
- Conditions
- Bronchial Diseases, Bronchiolitis, Bronchiolitis Obliterans, +32 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Lentiviral Gene Therapy for CGD
NCT03645486
- Conditions
- Chronic Disease, Chronic Granulomatous Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
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- Shenzhen Geno-immune Medical Institute Shenzhen, Guangdong, China
NCT07284641
- Conditions
- 22q11 Deletion Syndrome, Abnormalities, Multiple, Blood Protein Disorders, +56 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
- Conditions
- Chronic Disease, Chronic Granulomatous Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT06876363
- Conditions
- Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, +12 more
- Locations
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- University of California, Los Angeles Los Angeles, California, United States
- University of California, San Francisco San Francisco, California, United States
- Johns Hopkins All Children's Hospital St. Petersburg, Florida, United States
- Boston Children's Hospital Boston, Massachusetts, United States
Prevalence of Antibodies and Cytokines in Participants With Chronic Granulomatous Disease
NCT06605378
- Conditions
- Chronic Disease, Chronic Granulomatous Disease (CGD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
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- Home-based telemedicine Montgomery, Alabama, United States
- Home-based telemedicine Phoenix, Arizona, United States
- Home-based telemedicine Little Rock, Arkansas, United States
- Home-based telemedicine Sacramento, California, United States
NCT04528355
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +119 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT01962415
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +125 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT03055247
- Conditions
- Chronic Disease, Chronic Granulomatous Disease X-linked (X-CGD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
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- Ospedale Pediatrico Bambino Gesù Rome, Lazio, Italy
- Ospedale San Raffaele Milan, Lombardy, Italy
Part B- G1X-CGD (Lentiviral Vector Transduced CD34+ Cells) in Patients With X-Linked Chronic Granulomatous Disease
NCT07113743
- Conditions
- Chronic Disease, Chronic Granulomatous Disease (CGD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
A Study of the Safety and Efficacy of Prime Editing (PM359) in Participants With p47phox Autosomal Recessive Chronic Granulomatous Disease (CGD )
NCT06559176
- Conditions
- Chronic Disease, Chronic Granulomatous Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
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- University of California Los Angeles Medical Center Los Angeles, California, United States
- NIH Clinical Center Bethesda, Maryland, United States
- The Children's Hospital at Tristar Medical Group/Sarah Cannon Center for Blood Cancers Nashville, Tennessee, United States
- CHU - Sainte Justine Hospital Montreal, Quebec, Canada
pCCLCHIM-p47 (Lentiviral Vector Transduced CD34 Plus Cells) in Patients With p47 Autosomal Recessive Chronic Granulomatous Disease (AR-CGD)
NCT06253507
- Conditions
- Autosomal Recessive, Chronic Disease, Chronic Granulomatous Disease, +15 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Sequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency Diseases
NCT01852370
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Chronic Disease, +35 more
- Locations
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- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
Haloperidol For Outpatient Symptom Management in Patients Diagnosed With Cannabinoid Hyperemesis Syndrome in the Emergrency Department
NCT07726069
- Conditions
- Albinism, Cannabinoid Hyperemesis Syndrome, Chediak-Higashi Syndrome, +15 more
- Locations
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- University of Illinois Hospital Chicago, Illinois, United States
Study of Voicing My CHOiCES as a Tool for Advanced Care Planning in Young Adults With Cancer
NCT02108028
- Conditions
- Cancer, Chronic Disease, Chronic Granulomatous Disease, +17 more
- Locations
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- Children's Hospital of Orange County Orange, California, United States
- Childrens National Medical Center Washington D.C., District of Columbia, United States
- Moffitt Cancer Center Tampa, Florida, United States
- The Johns Hopkins Hospital Baltimore, Maryland, United States