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NCT02991144
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +12 more
- Locations
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- The Children's Hospital Colorado Aurora, Colorado, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Icahn School of Medicine at Mount Sinai New York, United States
- University Hospital Cleveland Medical Center/Case Western Reserve University Cleveland, Ohio, United States
Active, Not Recruiting
Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC Deficiency
NCT03636438
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +12 more
- Locations
-
- The Children's Hospital Colorado Aurora, Colorado, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Icahn School of Medicine New York, United States
- University Hospital Cleveland Medical Center/Case Western Reserve University Cleveland, Ohio, United States