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NCT07729982
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Eye Diseases, +13 more
- Locations
-
- Department of Ophthalmology, LMU University Hospital, LMU Medizin, Ludwig-Maximilians-Universität München Munich, Bavaria, Germany
NCT06970106
- Conditions
- Autosomal Dominant Optic Atrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, +16 more
- Locations
-
- Save Sight Institute - Sydney Eye Hospital Sydney, New South Wales, Australia
- Cerulea Clinical Trials East Melbourne, Australia
- Retina Specialists Auckland, New Zealand
Recruiting
Stem Cell Ophthalmology Treatment Study II
NCT03011541
- Conditions
- Abnormalities, Multiple, Age-Related Macular Degeneration, Autoimmune Diseases, +75 more
- Locations
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- MD Stem Cells Westport, Connecticut, United States
- MD Stem Cells Coral Springs, Florida, United States
- MD Stem Cells Kobinia Med Vienna, Austria
- The Saudi-German Hospital Dubai, United Arab Emirates
Recruiting
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
- Conditions
- 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
- Locations
-
- Sanford Health Sioux Falls, South Dakota, United States
- Online Patient Enrollment System Sydney, Australia
NCT00804102
- Conditions
- Arterial Occlusive Diseases, Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +35 more
- Locations
-
Not specified
Active, Not Recruiting
SAD of IVT PYC-001 in OPA1 Mutation-Associated Autosomal Dominant Optic Atrophy (Sundew)
NCT06461286
- Conditions
- Autosomal Dominant Optic Atrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, +16 more
- Locations
-
- Save Sight Institute - Sydney Eye Hospital Sydney, New South Wales, Australia
- Center for Eye Research Australia (CERA) East Melbourne, Victoria, Australia