Recruiting Oral Health, Saliva Viscosity and Composition in Oculo-Pharyngeal Muscular Dystrophy (OPMD) NCT07118280 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Muscular Diseases, +7 more Locations Sheba Medical Center — Ramat Gan, Israel View Trial Details
Recruiting A Study to Evaluate the Safety and Clinical Activity of Intramuscular Doses of BB-301 Administered to Subjects With Oculopharyngeal Muscular Dystrophy With Dysphagia NCT06185673 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Muscular Diseases, +7 more Locations NYU Langone Health — New York, United States View Trial Details
Completed Screening in Oculopharyngeal Muscular Dystrophy NCT02877784 Conditions Articulation Disorders, Communication Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +22 more Locations University of Florida — Gainesville, Florida, United States View Trial Details
Completed Safety Tolerability and Efficacy Study of Cabaletta to Treat Oculopharyngeal Muscular Dystrophy (OPMD) Patients NCT02015481 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Muscular Diseases, +7 more Locations UCLA — Los Angeles, California, United States Tahseen Mozaffar — Orange, California, United States Montreal Neurological Institute, McGill University — Montreal, Quebec, Canada Hadassah medical center — Jerusalem, Israel View Trial Details