Recruiting A Longitudinal Natural History Study of OPA1-Associated Autosomal-Dominant Optic Atrophy NCT07729982 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Eye Diseases, +13 more Locations Department of Ophthalmology, LMU University Hospital, LMU Medizin, Ludwig-Maximilians-Universität München — Munich, Bavaria, Germany View Trial Details
Recruiting Safety of Single and Repeat Dose of PYC-001 Eye Injections in People With Autosomal Dominant Optic Atrophy (Myrtle) NCT06970106 Conditions Autosomal Dominant Optic Atrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, +16 more Locations Save Sight Institute - Sydney Eye Hospital — Sydney, New South Wales, Australia Cerulea Clinical Trials — East Melbourne, Australia Retina Specialists — Auckland, New Zealand View Trial Details
Active, Not Recruiting SAD of IVT PYC-001 in OPA1 Mutation-Associated Autosomal Dominant Optic Atrophy (Sundew) NCT06461286 Conditions Autosomal Dominant Optic Atrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, +16 more Locations Save Sight Institute - Sydney Eye Hospital — Sydney, New South Wales, Australia Center for Eye Research Australia (CERA) — East Melbourne, Victoria, Australia View Trial Details