Recruiting Shwachman-Diamond Syndrome Global Patient Survey and Partnering Platform NCT06999954 Conditions Bone Marrow Diseases, Bone Marrow Failure Disorders, Cognitive Delay, Mild, +54 more Locations Shwachman-Diamond Syndrome Alliance Inc. — Woburn, Massachusetts, United States View Trial Details
Enrolling by Invitation Sequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency Diseases NCT01852370 Conditions Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Chronic Disease, +35 more Locations Children's Hospital of Pittsburgh of UPMC — Pittsburgh, Pennsylvania, United States View Trial Details