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NCT01873924
- Conditions
- Batten Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +19 more
- Locations
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- University of Rochester Rochester, New York, United States
Active, Not Recruiting
Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients
NCT04098211
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +11 more
- Locations
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- Children's Hospital of Orange County Orange, California, United States