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Recruiting
Italian NCL Registry: a Registry for NCL as an Integration Tool for Future Therapeutic Strategies
NCT06844877
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
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- IRCCS Fondazione Stella Maris Pisa, Italy
NCT01873924
- Conditions
- Batten Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +19 more
- Locations
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- University of Rochester Rochester, New York, United States
NCT04613089
- Conditions
- Batten Disease, CLN1 Disease, CLN10 Disease, +27 more
- Locations
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- University Medical Center Hamburg-Eppendorf Hamburg, Germany
Not Yet Recruiting
Gene Therapy Trial for CLN6 Batten Disease
NCT07582484
- Conditions
- Batten Disease, Batten's Disease, CLN6, +14 more
- Locations
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- University of California, San Diego - Rady Children's La Jolla, California, United States
NCT01966757
- Conditions
- Batten's Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyssomnias, +17 more
- Locations
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- Nationwide Children's Hospital Columbus, Ohio, United States
NCT00337636
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
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- Oregon Health and Science University Portland, Oregon, United States