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Recruiting
Neurogenetics Patient Registry
NCT02995538
- Conditions
- Neurogenetic Disorders
- Locations
-
- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
Not Yet Recruiting
Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47)
NCT06948019
- Conditions
- AP4B1, Central Nervous System Diseases, Congenital Abnormalities, +31 more
- Locations
-
- Boston Children's Hospital Boston, Massachusetts, United States