Recruiting A Phase 3 Study of NTLA-2001 in ATTRv-PN NCT06672237 Conditions Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, +23 more Locations Hospital Británico de Buenos Aires — Buenos Aires, Argentina Hospital Italiano de Buenos Aires (HIBA) — Buenos Aires, Argentina Hospital El Cruce — San Juan Bautista, Argentina Hospital das Clinicas da Universidade Estadual de Campinas (UNICAMP) — Campinas, Brazil View all 14 locations View more locations Show fewer locations Loading locations... View Trial Details
Recruiting Molecular and Functional Imaging in Monogenic PD. NCT05518617 Conditions Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +12 more Locations University Of Exeter — Exeter, Devon, United Kingdom View Trial Details
Not Yet Recruiting MCLENA-2: A Phase II Clinical Trial for the Assessment of Lenalidomide in Patients With Mild Cognitive Impairment NCT06177028 Conditions Alzheimer Disease, Amyloid Plaque, Brain Diseases, +24 more Locations Not specified View Trial Details
Completed Natural History Study of SLC25A46 Mutation-related Mitochondriopathy NCT04594590 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Eye Diseases, +13 more Locations UBMD Pediatrics — Buffalo, New York, United States View Trial Details
Completed Natural History Study of FDXR Mutation-related Mitochondriopathy NCT04580979 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Eye Diseases, +15 more Locations UBMD Pediatrics — Buffalo, New York, United States View Trial Details