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NCT06910813
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Fanconi Syndrome, +13 more
- Locations
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- University of California at San Diego - Rady Children's Hospital San Diego, California, United States
- Stanford University - Stanford Children's Health Stanford, California, United States
- Emory University School of Medicine - Children's Healthcare of Atlanta (recuiting Cohort 0) Atlanta, Georgia, United States
- Baylor College of Medicine - Texas Children's Hospital (recuiting Cohort 0) Houston, Texas, United States
Recruiting
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
- Conditions
- 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
- Locations
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- Sanford Health Sioux Falls, South Dakota, United States
- Online Patient Enrollment System Sydney, Australia
Recruiting
CYSTEA-BONE Clinical Study
NCT03919981
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Genetic Diseases, Inborn, +5 more
- Locations
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- CHU de Besançon Besançon, France
- CHU Bordeaux - Hôpital Pellegrin tripode Bordeaux, France
- Hôpital Femme Mère Enfant Bron, France
- Hôpital Jeanne de Flandre Lille, France
NCT01432561
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Genetic Diseases, Inborn, +5 more
- Locations
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- University of California, San Diego Center for Clinical Research Services (CCR) La Jolla, California, United States