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Published and searchable clinical trials

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Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
Locations
  • Stanford University/Lucile Packard Children's Hospital Palo Alto, California, United States
  • National Institute of Health Bethesda, Maryland, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
  • St Jude Children's Research Hospital Memphis, Tennessee, United States
Conditions
Muscular Diseases, Musculoskeletal Diseases, Myopathies, Nemaline, +4 more
Locations
  • Department of Paediatric Neurology - Neuromuscular Service, Evelina Children's Hospital London, United Kingdom
  • Dubowitz Neuromuscular Centre, UCL Great Ormond Street Hospital London, United Kingdom
  • John Walton Muscular Dystrophy Research Centre, Newcastle University Newcastle, United Kingdom
  • MDUK Oxford Neuromuscular Centre, University of Oxford Oxford, United Kingdom