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Recruiting
Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
NCT07700225
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +20 more
- Locations
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- Virginia Commonwealth University Richmond, Virginia, United States
NCT00082108
- Conditions
- Congenital Myotonic Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, +18 more
- Locations
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- University of Rochester Medical Center, Department of Neurology Rochester, New York, United States
NCT05027269
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +15 more
- Locations
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- University of California Los Angeles Los Angeles, California, United States
- Stanford University Palo Alto, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
Active, Not Recruiting
Global Study of Del-desiran for the Treatment of DM1
NCT06411288
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +21 more
- Locations
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- Stanford University Stanford, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
- University Research Center of South Florida Tampa, Florida, United States