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Published and searchable clinical trials
Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
NCT07700225
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +20 more
- Locations
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- Virginia Commonwealth University Richmond, Virginia, United States
NCT03981575
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
- Locations
-
- University of California, San Diego La Jolla, California, United States
- University of California, Los Angeles Los Angeles, California, United States
- University of Colorado - Denver Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
NCT06667453
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
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- University of Calgary Calgary, Alberta, Canada
- Ottawa Hospital Research Institute (OHRI) Ottawa, Ontario, Canada
- CIUSSS du Saguenay-Lac-Saint-Jean Chicoutimi, Quebec, Canada
- Montreal Neurological Institute Montreal, Quebec, Canada
An Open-Label Extension Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1 (FREEDOM-OLE)
NCT07220603
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
-
- University of Calgary Calgary, Alberta, Canada
- Ottawa Hospital Research Institute Ottawa, Ontario, Canada
- CIUSSS du Saguenay-Lac-Saint-Jean Saguenay, Canada
Study of ATX-01 in Participants With DM1
NCT06300307
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
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- UCLA Los Angeles, California, United States
- University of Florida Gainesville, Florida, United States
- University of Iowa Health Care - Department of Neurology Iowa City, Iowa, United States
- University of Kansas Medical Center, Department of Neurology Fairway, Kansas, United States
NCT07385443
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +14 more
- Locations
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- Hospitals within the DM1 network Multiple Locations, Andalusia, Spain
- Hospitals within the DM1 network Multiple Locations, Basque Country, Spain
- Hospitals within the DM1 network Multiple Locations, Canary Islands, Spain
- Hospitals within the DM1 network Multiple Locations, Cantabria, Spain
NCT05532813
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +12 more
- Locations
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- Neurology Department, Raymond-Poincaré hospital - APHP Garches, France
NCT06138743
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
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- Research Site Liverpool, New South Wales, Australia
- Research Site Birtinya, Queensland, Australia
- Research Site Herston, Queensland, Australia
- Research Site Melbourne, Victoria, Australia
NCT07136844
- Conditions
- Ataxia, Ataxia, Spinocerebellar, Autoimmune Diseases, +70 more
- Locations
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- Centre de référence des maladies neuromusculaire, Centre Hospitalier Régional de la Citadelle Liège, Belgium
Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study
NCT05982119
- Conditions
- Centronuclear Myopathy, Charcot-Marie-Tooth, Charcot-Marie-Tooth Disease, +25 more
- Locations
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- CHR de la Citadelle Liège, Belgium
- Fakultni nemocnice v Motole Prague, Czechia
- Galaa Military Medical Complex Cairo, Egypt
- Semmelweis University 2nd Department of Paediatrics Budapest, Hungary
Myotonic Dystrophy Family Registry
NCT02398786
- Conditions
- Congenital Myotonic Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dystrophia Myotonica, +24 more
- Locations
-
- Myotonic Dystrophy Foundation Oakland, California, United States
Global Open-Label Extension Study of Del-desiran for the Treatment of DM1
NCT07008469
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +19 more
- Locations
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- University of California, Los Angeles (UCLA) Los Angeles, California, United States
- Stanford University Stanford, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
Chinese Multicenter Clinical Outcome Cohort Study of Myotonic Dystrophy Type 1 (C-DMCOS-DM1)
NCT06101940
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
-
- Chinese People's Liberation Army General Hospital Beijing, Beijing Municipality, China
- Peking University First Hospital Beijing, Beijing Municipality, China
- First Affiliated Hospital of Chongqing Medical University Chongqing, Chongqing Municipality, China
- Fujian Medical University Union Hospital Fuzhou, Fujian, China
The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period.
NCT07072676
- Conditions
- Autoimmune Diseases, Autoimmune Diseases of the Nervous System, Brain Diseases, +69 more
- Locations
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- Medical Park, Bad Feilnbach, Reithofpark Bad Feilnbach, Germany
NCT07732439
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +11 more
- Locations
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- Centre hospitalier Universitaire d'Angers Angers, France
- CHU de Lille - Hôpital Lille, France
- CHU LA TIMONE - Service des Maladies Marseille, France
- Centre de référence des maladies neuromusculaires Nantes, France
Calcium Channel Blocker in Myotonic Dystrophy Type 1
NCT07075965
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
-
Not specified
NCT05027269
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +15 more
- Locations
-
- University of California Los Angeles Los Angeles, California, United States
- Stanford University Palo Alto, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
Safety, Tolerability, PK, and PD Study of PGN-EDODM1 in Participants With Myotonic Dystrophy Type 1
NCT06204809
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
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- UCI Center for Clinical Research Irvine, California, United States
- Stanford University Palo Alto, California, United States
- Rare Disease Research Atlanta, Georgia, United States
- University of Kansas Medical Center Fairway, Kansas, United States
Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients
NCT05479981
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
- Locations
-
- University of California Los Angeles Los Angeles, California, United States
- Stanford University Palo Alto, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
NCT03424460
- Conditions
- Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Embolism, +24 more
- Locations
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- Service de Cardiologie - Hôpital Cochin Paris, Île-de-France Region, France