Recruiting Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO) NCT07608432 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne Muscular Dystrophy (DMD), +21 more Locations Rare Disease Research, LLC — Hillsborough, North Carolina, United States View Trial Details
Not Yet Recruiting A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese Children NCT07511920 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +10 more Locations West China Second University Hospital, Sichuan University — Chengdu, China View Trial Details