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Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Motor Neuron Disease, +11 more
Locations
  • National Institutes of Health Clinical Center Bethesda, Maryland, United States
  • University of Mali Bamako, Mali
Conditions
Amyotrophic Lateral Sclerosis, Brain Diseases, Brain Infarction, +38 more
Locations
  • University of California, Davis Sacramento, California, United States
  • Stanford University School of Medicine Stanford, California, United States
  • Emory University School of Medicine Atlanta, Georgia, United States
  • Massachusetts General Hospital Boston, Massachusetts, United States

NCT05644522

Conditions
Autoimmune Diseases, Autoimmune Diseases of the Nervous System, Brain Diseases, +39 more
Locations
  • Shirley Ryan AbilityLab Chicago, Illinois, United States
Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, FKRP, FKRP Mutation, +17 more
Locations
  • University of California - Irvine Irvine, California, United States
  • University of Iowa Iowa City, Iowa, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
  • Kennedy Krieger Institute Baltimore, Maryland, United States
Conditions
Amyotrophic Lateral Sclerosis, Central Nervous System Diseases, Charcot-Marie-Tooth Disease, +28 more
Locations
  • Nemours Children's Hospital Delaware Wilmington, Delaware, United States
  • Nemours Children's Specialty Care Jacksonville, Florida, United States
  • Nemours Children's Hospital Orlando Orlando, Florida, United States