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Published and searchable clinical trials
NCT07486934
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +18 more
- Locations
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- UCSD - Altman Clinical and Translational Research Institute La Jolla, California, United States
- Rare Disease Research, LLC Atlanta, Georgia, United States
- IU Health Neuroscience Center Indianapolis, Indiana, United States
- Roy Blunt NextGen Precision Health Institute Columbia, Missouri, United States
NCT06817382
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- USA012 Little Rock, Arkansas, United States
- USA010 Davis, California, United States
- USA009 Los Angeles, California, United States
- USA002 Palo Alto, California, United States
NCT07674758
- Conditions
- Becker Muscular Dystrophy, Cardiomyopathies, Cardiomyopathy, +14 more
- Locations
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- UC Davis Sacramento, California, United States
- Children's National Washington D.C., District of Columbia, United States
- Lurie Children's Chicago, Illinois, United States
- Riley Children's Hospital Indianapolis, Indiana, United States
NCT07038200
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, FSH Muscular Dystrophy, FSHD, +25 more
- Locations
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- University of California Irvine Orange, California, United States
- Stanford University Palo Alto, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
NCT07700225
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +20 more
- Locations
-
- Virginia Commonwealth University Richmond, Virginia, United States
NCT05933057
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Universitaire Ziekenhuizen Leuven Leuven, Belgium
- British Columbia Children's Hospital Vancouver, British Columbia, Canada
- The University of Western Ontario - Children's Health Research Institute London, Ontario, Canada
- University of Ottawa - Children's Hospital of Eastern Ontario Ottawa, Ontario, Canada
NCT06998134
- Conditions
- Brain Damage, Chronic, Brain Diseases, Central Nervous System Diseases, +20 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT07172971
- Conditions
- Cardiomyopathies, Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
-
- Vanderbilt University Medical Center Nashville, Tennessee, United States
NCT07287189
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne, +10 more
- Locations
-
- University of California Los Angeles Los Angeles, California, United States
- Colorado Children's Aurora, Colorado, United States
- Lurie Children's Chicago, Illinois, United States
- UMass Memorial Medical Center Worcester, Massachusetts, United States
NCT06564974
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- Phoenix Children's Hospital Phoenix, Arizona, United States
- Arkansas Childrens Hospital Little Rock, Arkansas, United States
- Loma Linda University Pediatric Subspecialty Clinics Loma Linda, California, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
NCT07711730
- Conditions
- Behavior, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +13 more
- Locations
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- University of Deusto Bilbao, Biscay, Spain
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
NCT07160634
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Neurology Rare Disease Center Flower Mound, Texas, United States
- Children's Hospital of the King's Daughters Norfolk, Virginia, United States
- The Children's Hospital of Westmead Sydney, New South Wales, Australia
Study of Inherited Neurological Disorders
NCT00004568
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Motor Neuron Disease, +11 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
- University of Mali Bamako, Mali
NCT07521930
- Conditions
- Amyotrophic Lateral Sclerosis, Amyotrophic Lateral Sclerosis (ALS), Brain Diseases, +42 more
- Locations
-
- Johns Hopkins Medicine Baltimore, Maryland, United States
NCT06138639
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- University of California, Los Angeles Medical Center Los Angeles, California, United States
- University of California, Davis Sacramento, California, United States
- University of California San Diego, California, United States
NCT07127978
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Duchene Muscular Dystrophy, +12 more
- Locations
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- Arkansas Children's Research Institute Little Rock, Arkansas, United States
- Children's National Hospital Washington D.C., District of Columbia, United States
- Ann and Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Boston Children's Hospital Boston, Massachusetts, United States
NCT07673809
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- Republican Scientific and Practical Center Mother and Child Minsk, Belarus
- Russian Children's Clinical Hospital Moscow, Russia
- National Medical Research Center for Children Moscow, Russia
- Veltischev Research and Clinical Institute for Pediatrics and Pediatric Surgery of the Pirogov Russian National Research Medical University Moscow, Russia
NCT04626674
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Stanford University Palo Alto, California, United States
- University of California, Davis Sacramento, California, United States
- Washington University in St. Louis St Louis, Missouri, United States
Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular Dystrophies
NCT07378553
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchene Muscular Dystrophy, +9 more
- Locations
-
- CHU de Nantes Nantes, France
NCT07429240
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy With Mutations Amenable to PBGENE-DMD, Genetic Diseases, Inborn, +8 more
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Washington University School of Medicine St Louis, Missouri, United States