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NCT04815005
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Genetic Diseases, Inborn, +12 more
- Locations
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- University of Pennsylvania Philadelphia, Pennsylvania, United States
- Department of Vascular Medicine, Amsterdam UMC Amsterdam, Netherlands
- Department of Medicine, Division of Lipidology and Hatter Institute for Cardiovascular Research in Africa, University of Cape Town Cape Town, South Africa
- c. Carbohydrate and Lipid Metabolism Research Unit, Faculty of Health Sciences, University of Witwatersrand Johannesburg, South Africa
NCT00001404
- Conditions
- Abnormalities, Multiple, Bone Diseases, Bone Diseases, Developmental, +28 more
- Locations
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- Cedars Sinai Medical Center Los Angeles, California, United States
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
- Greenwood Genetics Center Greenwood, South Carolina, United States
- Ankara University School of Medicine Ankara, Turkey (Türkiye)
NCT00465985
- Conditions
- Chronic Disease, Chronic Inducible Urticaria, Chronic Urticaria, +18 more
- Locations
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- Novartis Investigative Site San Francisco, California, United States
- Novartis Investigative Site Chicago, Illinois, United States
- Novartis Investigative Site Madison, Wisconsin, United States
- Novartis Investigative Site Le Kremlin-Bicêtre, France
- Conditions
- Chronic Disease, Chronic Inducible Urticaria, Chronic Urticaria, +21 more
- Locations
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- Little Rock Allergy and Asthma Clinic Little Rock, Arkansas, United States
- UCSF School of Medicine San Francisco, California, United States
- Allergy Center at Brookstone Columbus, Georgia, United States
- Rush-Presbyterian St. Lukes Medical Center Chicago, Illinois, United States
NCT01114815
- Conditions
- Brain Diseases, Brain Infarction, Brain Ischemia, +22 more
- Locations
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- NYU School of Medicine New York, United States
Active, Not Recruiting
A Study to Evaluate the Safety and Tolerability of QR-1123 in Subjects With Autosomal Dominant Retinitis Pigmentosa Due to the P23H Mutation in the RHO Gene
NCT04123626
- Conditions
- Autosomal Dominant Retinitis Pigmentosa, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, +17 more
- Locations
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- Sue Anschutz-Rogers Eye Center, University of Colorado - Dept. of Ophthalmology Aurora, Colorado, United States
- VitreoRetinal Associates Gainesville, Florida, United States
- Shriners UK Ophthalmology - University of Kentucky Lexington, Kentucky, United States
- Casey Eye Institute, OHSU Portland, Oregon, United States