Recruiting ISP-001: Sleeping Beauty Transposon-Engineered B Cells for MPS I NCT05682144 Conditions Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +11 more Locations UCSF Benioff Children's Hospital Oakland — Oakland, California, United States University of Minnesota — Minneapolis, Minnesota, United States View Trial Details