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A Phase I/II Trial of JR-446 in Mucopolysaccharidosis Type IIIB (MPS IIIB)
NCT07640984
- Conditions
- Mucopolysaccharidosis IIIB
- Locations
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- Children's Hospital Oakland Research Institution, Attn: 2900 Wing Oakland, California, United States
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
- Lysosomal and Rare Disorders Research and Treatment Center (LDRTC) Fairfax, Virginia, United States
- University Medical Center Hamburg-Eppendorf Hamburg, Germany
NCT02324049
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
- Locations
-
- Minneapolis, Minnesota, United States
- Pittsburgh, Pennsylvania, United States
- Barcelona, Spain
- Birmingham, United Kingdom