Recruiting An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB NCT06488924 Conditions Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more Locations Hiroshima University Hospital — Hiroshima, Japan University of the Ryukyus Hospital — Okinawa, Japan National Center for Child Health and Development — Tokyo, Japan View Trial Details
Enrolling by Invitation ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program NCT05368038 Conditions Acid Sphingomyelinase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +65 more Locations Maimonides Medical Center — Brooklyn, New York, United States NYU Langone Hospital - Brooklyn — Brooklyn, New York, United States North Shore University Hospital — Manhasset, New York, United States NYU Langone Health - Tisch Hospital — New York, United States View more locations Show fewer locations Loading locations... View Trial Details
