Recruiting Longitudinal Study of Neurodegenerative Disorders NCT03333200 Conditions ALD, Alpha-Mannosidosis, Batten Disease, +78 more Locations UPMC Children's Hospital of Pittsburgh — Pittsburgh, Pennsylvania, United States View Trial Details
Completed Establishment of Human Cellular Disease Models for Morquio Disease NCT03872713 Conditions Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more Locations Childrens Hospital and Institute of Child Health, Ferozepur Road — Lahore, Pakistan View Trial Details
Completed Pregnancy With Morquio Syndrome - What Are Patients' Perspectives and Has ERT Changed Them? NCT03150069 Conditions Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +11 more Locations Emory University — Decatur, Georgia, United States View Trial Details
Completed Psychological Concomitants of Morquio Syndrome (The MAP Study) NCT01752296 Conditions Behavior, Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more Locations Emory University — Decatur, Georgia, United States View Trial Details
