Completed Safety & Efficacy Study of ORGN001 (Formerly ALXN1101) in Pediatric Patients With MoCD Type A Currently Treated With rcPMP NCT02047461 Conditions Molybdenum Cofactor Deficiency, Complementation Group A, Molybdenum Cofactor Deficiency, Type A, Molybdenum cofactor deficiency Locations Children's Hospital of Wisconsin — Milwaukee, Wisconsin, United States Monash Medical Centre — Melbourne, Australia Beatrix Children's Hospital — Groningen, Netherlands Unité des maladies métaboliques — Tunis, Tunisia View more locations Show fewer locations Loading locations... View Trial Details
Completed Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A NCT02629393 Conditions Molybdenum Cofactor Deficiency, Complementation Group A, Molybdenum Cofactor Deficiency, Type A, Molybdenum cofactor deficiency Locations Children's Hosptial of Michigan — Detroit, Michigan, United States Cincinnati Children's Hospital Medical Center — Cincinnati, Ohio, United States Children's Hospital of Wisconsin — Milwaukee, Wisconsin, United States HaEmek Medical Center — Afula, Israel View more locations Show fewer locations Loading locations... View Trial Details
Active, Not Recruiting Early Check: Expanded Screening in Newborns NCT03655223 Conditions 17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more Locations RTI International — Research Triangle Park, North Carolina, United States View Trial Details
