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NCT07398508
- Conditions
- Autonomic Nervous System Diseases, Brain Diseases, Brain Diseases, Metabolic, +26 more
- Locations
-
- Vagelos College of Physicians and Surgeons, Columbia University New York, United States
NCT04977388
- Conditions
- Autonomic Nervous System Diseases, Brain Diseases, Brain Diseases, Metabolic, +22 more
- Locations
-
- Vagelos College of Physicians and Surgeons, Columbia University New York, United States
NCT00811785
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +25 more
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
NCT00001262
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +22 more
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
Active, Not Recruiting
Early Check: Expanded Screening in Newborns
NCT03655223
- Conditions
- 17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
- Locations
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- RTI International Research Triangle Park, North Carolina, United States
Active, Not Recruiting
Long Term Follow-up on Menkes Disease Patients
NCT04337684
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Sentynl Therapeutics Solana Beach, California, United States