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NCT02231697
- Conditions
- Males With X-linked Myotubular Myopathy (XLMTM), Muscular Diseases, Musculoskeletal Diseases, +3 more
- Locations
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- Cure CMD San Pedro, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- University of Florida - Gainesville, Children's Research Institute Gainesville, Florida, United States
- Lurie Children's Hospital Chicago, Illinois, United States