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NCT05284006
- Conditions
- Bone Diseases, Bone Diseases, Developmental, Carbohydrate Metabolism, Inborn Errors, +17 more
- Locations
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- Nemours Children's Health, Delaware Valley Wilmington, Delaware, United States
NCT04532047
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +39 more
- Locations
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- University of California San Francisco, California, United States
Recruiting
Cardiac Structure and Function in MPS
NCT07361536
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +13 more
- Locations
-
- Children'S Hospital of Orange County Orange, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Saint Louis University St Louis, Missouri, United States
NCT02294877
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Children's Hospital of Los Angeles Los Angeles, California, United States
- University of Southern California Los Angeles, California, United States
NCT01415427
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
- Locations
-
- Phoenix, Arizona, United States
- Oakland, California, United States
- Orange, California, United States
- Wilmington, Delaware, United States
Completed
Gait Analysis in MPS IVA
NCT01920828
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +11 more
- Locations
-
- Oregon Health and Science University Portland, Oregon, United States
NCT01515956
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
- Locations
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- Oakland, California, United States
- Manhasset, New York, United States
- Monza, Italy
- Taipei, Taiwan
NCT01961518
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +14 more
- Locations
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- Greenwood Genetic Center Greenville, South Carolina, United States
Active, Not Recruiting
Safety and Efficacy of Voxzogo for Growth Deficits in MPS IVA and VI
NCT05845749
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
- Locations
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- UCSF Benioff Children's Hospital Oakland Oakland, California, United States