Recruiting Cardiac Structure and Function in MPS NCT07361536 Conditions Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +13 more Locations Children'S Hospital of Orange County — Orange, California, United States University of Minnesota — Minneapolis, Minnesota, United States Saint Louis University — St Louis, Missouri, United States View Trial Details
Completed Pregnancy With Morquio Syndrome - What Are Patients' Perspectives and Has ERT Changed Them? NCT03150069 Conditions Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +11 more Locations Emory University — Decatur, Georgia, United States View Trial Details