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Showing 1–11 of 11 trials

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Published and searchable clinical trials

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Conditions
Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy With Fatty Liver and Infantile-onset Cataract Caused by TRAPPC11 Mutations), Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy With Hypoglycosylation of Dystroglycan and Epilepsy), Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy With Hypoglycosylation of Dystroglycan), +89 more
Locations
  • Congenital Muscle Disease International Registry (www.cmdir.org) Lakewood, California, United States
Conditions
Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, +12 more
Locations
  • Washington D.C., District of Columbia, United States
  • Kansas City, Kansas, United States
  • Baltimore, Maryland, United States
  • Boston, Massachusetts, United States
Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb-girdle Muscular Dystrophy, +7 more
Locations
  • University of California, San Diego-Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Nationwide Childrens Hospital Columbus, Ohio, United States
  • The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
  • Children's Hospital of The King's Daughter Norfolk, Virginia, United States
Conditions
Cardiomyopathies, Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • Barrow Neurological Institute Phoenix, Arizona, United States
  • Arkansas Children's Little Rock, Arkansas, United States
  • University of California San Diego La Jolla, California, United States
  • University of California, Davis Health Dept of PM&R Sacramento, California, United States
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