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Published and searchable clinical trials
NCT07711730
- Conditions
- Behavior, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +13 more
- Locations
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- University of Deusto Bilbao, Biscay, Spain
NCT00390104
- Conditions
- Atrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne/Becker Muscular Dystrophy, +20 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States
NCT01403402
- Conditions
- Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy With Fatty Liver and Infantile-onset Cataract Caused by TRAPPC11 Mutations), Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy With Hypoglycosylation of Dystroglycan and Epilepsy), Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy With Hypoglycosylation of Dystroglycan), +89 more
- Locations
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- Congenital Muscle Disease International Registry (www.cmdir.org) Lakewood, California, United States
Weekly Steroids in Muscular Dystrophy
NCT04054375
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
- Locations
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- Northwestern University Chicago, Illinois, United States
NCT00457912
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb-girdle Muscular Dystrophy, +7 more
- Locations
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- Nationwide Children's Hospital Columbus, Ohio, United States
NCT02759302
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb-girdle Muscular Dystrophy, +7 more
- Locations
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- Copenhagen Neuromuscular Center, Rigshospitalet Copenhagen, Denmark
NCT02635321
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb-girdle Muscular Dystrophy, +7 more
- Locations
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- Copenhagen Neuromuscular Center Copenhagen, Denmark
NCT00873782
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, +11 more
- Locations
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- University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
NCT00104078
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, +12 more
- Locations
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- Washington D.C., District of Columbia, United States
- Kansas City, Kansas, United States
- Baltimore, Maryland, United States
- Boston, Massachusetts, United States
A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4
NCT06246513
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb-girdle Muscular Dystrophy, +7 more
- Locations
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- University of California, San Diego-Altman Clinical and Translational Research Institute La Jolla, California, United States
- Nationwide Childrens Hospital Columbus, Ohio, United States
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- Children's Hospital of The King's Daughter Norfolk, Virginia, United States
A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice
NCT04475926
- Conditions
- Cardiomyopathies, Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- Barrow Neurological Institute Phoenix, Arizona, United States
- Arkansas Children's Little Rock, Arkansas, United States
- University of California San Diego La Jolla, California, United States
- University of California, Davis Health Dept of PM&R Sacramento, California, United States