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NCT03333200
- Conditions
- ALD, Alpha-Mannosidosis, Batten Disease, +78 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT03639285
- Conditions
- Leukodystrophy
- Locations
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- Primary Children's Hospital Salt Lake City, Utah, United States
Recruiting
The Myelin Disorders Biorepository Project
NCT03047369
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
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- Children's Hospital of Los Angeles Los Angeles, California, United States
- Children's Hospital of Orange County Orange, California, United States
- Stanford University (Lucile Packard Children's Hospital) Palo Alto, California, United States
- University of California, Davis (UC Davis Health) Sacramento, California, United States
Recruiting
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
- Conditions
- 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
- Locations
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- Sanford Health Sioux Falls, South Dakota, United States
- Online Patient Enrollment System Sydney, Australia
NCT05443906
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +33 more
- Locations
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- Kennedy Krieger Institute Baltimore, Maryland, United States
NCT02699190
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
-
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT00889174
- Conditions
- Brain Diseases, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +5 more
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States