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Recruiting
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
- Conditions
- 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
- Locations
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- Sanford Health Sioux Falls, South Dakota, United States
- Online Patient Enrollment System Sydney, Australia
NCT03137355
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
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- The University of Texas Health Science Center at Houston Houston, Texas, United States
Enrolling by Invitation
Sirolimus for Leigh Syndrome
NCT06843811
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +12 more
- Locations
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- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT02352896
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +12 more
- Locations
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- Gregory Enns Stanford University, California, United States
- Akron Children's Hospital Akron, Ohio, United States
- Baylor College of Medicine Houston, Texas, United States
- Seattle Children's Hospital Seattle, Washington, United States
NCT01721733
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +12 more
- Locations
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- Stanford University Palo Alto, California, United States
- Akron Children's Hospital Akron, Ohio, United States
- Baylor College of Medicine Houston, Texas, United States
- Seattle Children's Hospital Seattle, Washington, United States