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Recruiting
Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)
NCT06891443
- Conditions
- Blindness, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +28 more
- Locations
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- UCSF Wayne and Gladys Valley Center for Vision San Francisco, California, United States
- University of Miami - Bascom Palmer Eye Institute Miami, Florida, United States
- University of Iowa Iowa City, Iowa, United States
- University of Minnesota Medical School Minneapolis, Minnesota, United States
NCT03396042
- Conditions
- Blindness, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +17 more
- Locations
-
- Bascom Palmer Eye Institute Miami, Florida, United States
- Massachusetts Eye and Ear Infirmary Boston, Massachusetts, United States
- W.K. Kellogg Eye Center Ann Arbor, Michigan, United States
- Casey Eye Institute - OHSU Portland, Oregon, United States
Active, Not Recruiting
A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)
NCT03913143
- Conditions
- Blindness, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +26 more
- Locations
-
- University of Iowa Iowa City, Iowa, United States
- Universitair Ziekenhuis Gent (UZ) Ghent, Belgium
- INRET Clínica/ Santa Casa de Misericórdia de Belo Horizonte Belo Horizonte, Minas Gerais, Brazil
- Federal University of São Paulo - Hospital São Paulo (UNIFESP-HSP) São Paulo, Brazil