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NCT07354724
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
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- University of California-Irvine Irvine, California, United States
- Duke University School of Medicine - Early Phase Research Unit Durham, North Carolina, United States
- The Lysosomal & Rare Disorders Research & Treatment Center Fairfax, Virginia, United States
NCT05431127
- Conditions
- Late-onset Pompe Disease, Lysosomal Disease
- Locations
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- Duke University Medical Center Durham, North Carolina, United States