Recruiting A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD) NCT07282847 Conditions Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more Locations Barrow Neurological Institute — Phoenix, Arizona, United States University of California, Irvine (UCI) — Irvine, California, United States Stanford Neuroscience Health Center — Palo Alto, California, United States NYU Langone — New York, United States View more locations Show fewer locations Loading locations... View Trial Details
Completed Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe Disease NCT03893240 Conditions Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +17 more Locations Barrow Neurological Institute — Phoenix, Arizona, United States University of California Irvine Health — Orange, California, United States University of Kansas Medical Center — Kansas City, Kansas, United States University of Minnesota Medical School — Minneapolis, Minnesota, United States View all 18 locations View more locations Show fewer locations Loading locations... View Trial Details
Active, Not Recruiting A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE) NCT04093349 Conditions Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +17 more Locations Barrow Neurological Institute — Phoenix, Arizona, United States University of California Irvine Health — Orange, California, United States Emory University School of Medicine — Atlanta, Georgia, United States University of Kansas Medical Center Research Institute — Kansas City, Kansas, United States View all 29 locations View more locations Show fewer locations Loading locations... View Trial Details
