Enrolling by Invitation Genetic Diagnosis in Inborn Errors of Metabolism NCT06376279 Conditions Brain Diseases, Central Nervous System Diseases, Epilepsy, +10 more Locations Not specified View Trial Details
Enrolling by Invitation Tissue Sample Study for Mitochondrial Disorders NCT01803906 Conditions Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +30 more Locations Columbia University — New York, United States View Trial Details
Completed A Dose-escalating Clinical Trial With KH176 NCT02544217 Conditions Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +26 more Locations Drug Research Unit Ghent — Ghent, Belgium View Trial Details