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NCT05230459
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, FKRP, FKRP Mutation, +17 more
- Locations
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- University of California - Irvine Irvine, California, United States
- University of Iowa Iowa City, Iowa, United States
- University of Kansas Medical Center Kansas City, Kansas, United States
- Kennedy Krieger Institute Baltimore, Maryland, United States
NCT05989620
- Conditions
- Cardiomyopathies, Cardiovascular Diseases, Cobblestone Lissencephaly, +70 more
- Locations
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- Virginia Commonwealth University Richmond, Virginia, United States
NCT02841267
- Conditions
- LGMD2I, Muscular Dystrophy, Limb-Girdle, Type 2I
- Locations
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- Hugo W. Moser Research Institute at Kennedy Krieger, Inc. Baltimore, Maryland, United States
Active, Not Recruiting
Study of BBP-418 in Patients With LGMD2I
NCT04800874
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, LGMD2I, +8 more
- Locations
-
- Virginia Commonwealth University Richmond, Virginia, United States