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LGMD R1 Natural History Study

NCT05618080

Conditions
Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
Locations
  • University of California, Irvine Orange, California, United States
  • University of Colorado Anschutz Medical Campus Aurora, Colorado, United States
  • University of Florida Gainesville, Florida, United States
  • The Community Health Clinic, Inc. Shipshewana, Indiana, United States