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NCT03999814
- Conditions
- Brain Diseases, Central Nervous System Diseases, INAD, +3 more
- Locations
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- Sarah Endemann Los Altos, California, United States
Active, Not Recruiting
A Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal Dystrophy
NCT03570931
- Conditions
- Brain Diseases, Central Nervous System Diseases, Infantile Neuroaxonal Dystrophy, +2 more
- Locations
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- University of California San Francisco, Benioff Children's Hospital San Francisco, California, United States
- Jacobs Levy Genomics and Research Program Morristown, New Jersey, United States